Share Your Insight to Help Develop New Potential PMD Therapies

Take a survey to help industry leaders understand what it’s like living with PMD and to help guide the development of new potential PMD therapies

In an effort to guide the development of new potential therapies for PMD, Ionis Pharmaceuticals is conducting a survey of people living with PMD and their caregivers. This survey is intended to help researchers better understand your most bothersome symptoms, the challenges in everyday life, your diagnostic journey and your perspective on participating in future clinical trials for PMD. 

Results from this survey will be summarized and shared with Ionis and regulatory agencies such as the U.S. Food and Drug Administration (FDA) to incorporate the perspective of people living with PMD in the drug development process. These efforts are to ensure that the patient voice is considered in the development and regulation of any new potential therapies.  

Results will be accessible to all participants. 

We kindly ask that you please take the time to fill out this important survey.